ASOs (tofersen for SOD1-ALS), gene therapy (AAV-aducanumab), tau-targeted antibodies, alpha-synuclein vaccines (PD03A); decades of failed trials inform current strategy.
ASOs (tofersen for SOD1-ALS), gene therapy (AAV-aducanumab), tau-targeted antibodies, alpha-synuclein vaccines (PD03A); decades of failed trials inform current strategy.